Luspatercept for non-deletional hemoglobin H disease

Pediatr Blood Cancer. 2024 Oct;71(10):e31224. doi: 10.1002/pbc.31224. Epub 2024 Jul 23.

Authors

Yuan-Ning Yang¹, Yen-Yin Chou¹, Chao-Neng Cheng¹

Affiliation

¹ Department of Pediatrics, National Cheng Kung University Hospital, College of Medicine, National Cheng Kung University, Tainan, Taiwan.

PMID: 39044307
DOI: 10.1002/pbc.31224

No abstract available

Publication types

Letter

MeSH terms

Activin Receptors, Type II / genetics
Activin Receptors, Type II / therapeutic use
Adolescent
Child
Child, Preschool
Female
Humans
Immunoglobulin Fc Fragments / therapeutic use
Male
Recombinant Fusion Proteins* / therapeutic use
alpha-Thalassemia* / drug therapy
alpha-Thalassemia* / genetics

Substances

luspatercept
Recombinant Fusion Proteins
Immunoglobulin Fc Fragments
Activin Receptors, Type II