Non-B DNA-informed mutation burden as a marker of treatment response and outcome in cancer

Br J Cancer. 2024 Dec;131(11):1825-1832. doi: 10.1038/s41416-024-02873-7. Epub 2024 Oct 19.

Abstract

Background: Genomic instability is crucial in tumorigenesis, with Tumour Mutation Burden (TMB) being a biomarker to indicate therapeutic effectiveness, particularly in immunotherapy. However, TMB is not always a reliable predictor and displays heterogeneity. Non-B DNA, susceptible to mutations, play a significant role in cancer development, indicating their potential merit when combined with mutation for enhanced markers in cancer.

Methods: We assessed mutations and non-B DNA interplay as biomarkers. Our methodology quantifies tumour mutations and their co-localization with non-B DNA, using survival and drug sensitivity assessments for clinical relevance.

Results: We introduce two novel markers, 'nbTMB' (non-B-informed tumour mutation burden) and 'mlTNB' (mutation-localised tumour non-B burden). In case studies: (1) nbTMB informs on survival heterogeneity among TMB-high patients undergoing immunotherapy whereas TMB is unable to further differentiate; (2) nbTMB informs on altered cisplatin sensitivity among ovarian cancer cell lines whereas TMB is unable to differentiate; and (3) mlTNB informs on survival heterogeneity among early-stage pancreatic cancer progressors in whom other markers of genomic instability fail to differentiate.

Conclusions: These novel markers offer a nuanced approach to enhance our understanding of treatment responses and outcomes in cancer, underscoring the need for a comprehensive exploration of the interplay between non-B and B-DNA features.

MeSH terms

  • Biomarkers, Tumor* / genetics
  • Cell Line, Tumor
  • Female
  • Genomic Instability
  • Humans
  • Immunotherapy / methods
  • Mutation*
  • Neoplasms* / drug therapy
  • Neoplasms* / genetics
  • Neoplasms* / therapy
  • Ovarian Neoplasms / drug therapy
  • Ovarian Neoplasms / genetics
  • Pancreatic Neoplasms / drug therapy
  • Pancreatic Neoplasms / genetics
  • Pancreatic Neoplasms / pathology
  • Treatment Outcome

Substances

  • Biomarkers, Tumor