Letter to the editor: "Levacetylleucine a game changer for Niemann pick disease type-C"

Brain Dev. 2024 Oct 21:S0387-7604(24)00135-9. doi: 10.1016/j.braindev.2024.10.002. Online ahead of print.
No abstract available

Keywords: Levacetylleucine; Lysosomal storage disease; N-acetyl-L-leucine (NALL); Niemann pick disease type-C (NPC).

Publication types

  • Letter