Characterization of RNA editing and gene therapy with a compact CRISPR-Cas13 in the retina

Affiliations

• ¹ Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia.
• ² Ophthalmology, Department of Surgery, University of Melbourne, East Melbourne, VIC 3002, Australia.
• ³ Menzies Institute for Medical Research, University of Tasmania, Hobart, TAS 7000, Australia.
• ⁴ Department of Optometry and Vision Sciences, University of Melbourne, Parkville, VIC 3052, Australia.
• ⁵ School of Medical Sciences, Faculty of Medicine and Health, University of Sydney, Camperdown, NSW 2050, Australia.
• ⁶ Stem Cell Medicine and Stem Cell and Organoid Facility, Children's Medical Research Institute, Faculty of Medicine and Health, University of Sydney, Westmead, NSW 2145, Australia.
• ⁷ Translational Vectorology Research Unit, Children's Medical Research Institute, Faculty of Medicine and Health, University of Sydney, Westmead, NSW 2145, Australia.
• ⁸ Laboratory of Molecular Oncology and Innovative Therapies, Military Institute of Medicine - National Research Institute, Warsaw 04-349, Poland.
• ⁹ Australian Genome Therapeutics Centre, Children's Medical Research Institute and Sydney Children's Hospitals Network, Westmead, NSW 2145, Australia.
• ¹⁰ Centre for Ophthalmology and Visual Science, University of Western Australia, Crawley, WA 6009, Australia.
• ¹¹ Eye Center, Zhongshan City People's Hospital, Zhongshan, Guangdong Province 528403, China.