HBV serum RNA kinetics during nucleic acid polymers based therapy predict functional cure

Antiviral Res. 2025 Feb:234:106061. doi: 10.1016/j.antiviral.2024.106061. Epub 2024 Dec 19.

Abstract

Serum HBV-RNA is proposed to be a circulating marker of cccDNA transcriptional activity in hepatocytes. The combination of tenofovir-disoproxil-fumarate (TDF) and pegylated-interferon-alpha-2a (pegIFN) with nucleic-acid polymer (NAP) treatment was associated with a relatively high rate of functional cure (FC) 48 weeks after discontinuation of all therapy. We aim to characterize HBV RNA kinetics under TDF and pegIFN ± NAP combination therapies. Forty participants with chronic HBV in the REP401 phase-II clinical trial received 48 weeks of triple combination therapy with NAPs, pegIFN, and TDF. For 20 participants, triple combination therapy (TDF + pegIFN + NAPs) followed 24 weeks of TDF. For 20 other participants, triple combination therapy followed 24 weeks of TDF monotherapy and 24 weeks of dual therapy (TDF + pegIFN). The Abbott RUO assay for HBV RNA (LLoQ = 1.65 logU/mL) was performed every 4 weeks. Previously unrecognized HBV RNA kinetic patterns were identified with dual/triple therapy including (i) no change (ii) an increase followed by a new elevated plateau (only under dual therapy) and (iii) a transient increase followed by a spontaneous decline. All participants establishing a new elevated HBV RNA plateau level experienced a subsequent monophasic decline following the introduction of NAPs. Failure to reach HBV RNA LLoQ by 16 weeks of triple therapy had a negative predictive value of 100% for FC. The median HBV RNA half-life for participants in the virological-rebound group was significantly (p = 0.01) longer than in the partial and FC groups (5.7 vs 2.7 weeks, respectively). Achieving partial/functional cure is associated with a shorter HBV RNA half-life, which could reflect faster inactivation of cccDNA transcriptional activity.

Keywords: Functional cure; HBV RNA; Hepatitis B virus; Nucleic-acid polymers; TDF; pegIFN.

Publication types

  • Clinical Trial, Phase II

MeSH terms

  • Adult
  • Antiviral Agents* / therapeutic use
  • Drug Therapy, Combination
  • Female
  • Hepatitis B virus* / drug effects
  • Hepatitis B virus* / genetics
  • Hepatitis B, Chronic* / blood
  • Hepatitis B, Chronic* / drug therapy
  • Hepatitis B, Chronic* / virology
  • Humans
  • Interferon-alpha* / therapeutic use
  • Kinetics
  • Male
  • Middle Aged
  • Polyethylene Glycols* / therapeutic use
  • Polymers / therapeutic use
  • RNA, Viral* / blood
  • Recombinant Proteins* / therapeutic use
  • Tenofovir* / therapeutic use
  • Treatment Outcome
  • Viral Load / drug effects

Substances

  • RNA, Viral
  • Antiviral Agents
  • Tenofovir
  • Interferon-alpha
  • Polyethylene Glycols
  • peginterferon alfa-2a
  • Recombinant Proteins
  • Polymers