Successful treatment of severe carbamyl phosphate synthetase I deficiency

Arch Dis Child. 1984 Dec;59(12):1183-5. doi: 10.1136/adc.59.12.1183.

Abstract

We describe a girl with neonatal hyperammonaemia due to carbamyl phosphate synthetase I deficiency. Treatment consisted of protein restriction from the second day of life. Sodium benzoate was given for three weeks after birth and again from 7 months of age together with sodium phenylacetate to improve protein tolerance. Growth and development are normal at 15 months of age.

Publication types

  • Case Reports

MeSH terms

  • Amino Acid Metabolism, Inborn Errors / diet therapy*
  • Amino Acid Metabolism, Inborn Errors / drug therapy
  • Ammonia / blood
  • Benzoates / therapeutic use
  • Benzoic Acid
  • Carbamoyl-Phosphate Synthase (Ammonia) / deficiency*
  • Dietary Proteins / administration & dosage
  • Female
  • Humans
  • Infant, Newborn
  • Ligases / deficiency*
  • Phenylacetates / therapeutic use

Substances

  • Benzoates
  • Dietary Proteins
  • Phenylacetates
  • Ammonia
  • Benzoic Acid
  • Ligases
  • Carbamoyl-Phosphate Synthase (Ammonia)
  • phenylacetic acid