Abstract
Peroxisomal bifunctional enzyme complex deficiency is a recently recognized abnormality of fatty acid metabolism. We herein present the association of a flecked retina with peroxisomal bifunctional enzyme deficiency, a clinical association not previously reported. We suggest the finding of a flecked retina in an infant presenting with hypotonia, seizures, and failure to thrive is highly suggestive of this diagnosis.
MeSH terms
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3-Hydroxyacyl CoA Dehydrogenases / deficiency*
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3-Hydroxyacyl CoA Dehydrogenases / genetics
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Diagnosis, Differential
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Enoyl-CoA Hydratase / deficiency*
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Enoyl-CoA Hydratase / genetics
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Failure to Thrive / complications
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Female
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Fundus Oculi
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Humans
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Infant, Newborn
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Isomerases / deficiency*
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Isomerases / genetics
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Microbodies / enzymology*
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Multienzyme Complexes / deficiency*
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Multienzyme Complexes / genetics
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Muscle Hypotonia / complications
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Peroxisomal Bifunctional Enzyme
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Retina / pathology*
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Retinal Diseases / complications
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Retinal Diseases / diagnosis
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Retinal Diseases / enzymology*
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Seizures / complications
Substances
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Multienzyme Complexes
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3-Hydroxyacyl CoA Dehydrogenases
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EHHADH protein, human
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Enoyl-CoA Hydratase
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Peroxisomal Bifunctional Enzyme
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Isomerases