Biochemical and immunological status following gene therapy and PEG-ADA therapy for adenosine deaminase (ADA) deficiency

Adv Exp Med Biol. 1994:370:391-4. doi: 10.1007/978-1-4615-2584-4_85.
No abstract available

Publication types

  • Case Reports
  • Comparative Study

MeSH terms

  • Adenosine Deaminase / biosynthesis
  • Adenosine Deaminase / deficiency*
  • Adenosine Deaminase / therapeutic use*
  • Female
  • Genetic Therapy*
  • Hematopoietic Stem Cells
  • Humans
  • Infant
  • Recombinant Proteins / biosynthesis
  • Severe Combined Immunodeficiency / drug therapy
  • Severe Combined Immunodeficiency / physiopathology
  • Severe Combined Immunodeficiency / therapy*
  • Transfection

Substances

  • Recombinant Proteins
  • Adenosine Deaminase
  • pegademase bovine