N-(acyloxyalkyl)pyridinium salts as soluble prodrugs of a potent platelet activating factor antagonist

J Med Chem. 1994 Dec 23;37(26):4423-9. doi: 10.1021/jm00052a001.

Abstract

Pyrrolothiazole 4 is a potent antagonist of platelet activating factor-mediated effects in a variety of in vitro and in vivo assays. Despite its positive activity in models of inflammation and septic shock, 4 lacks the aqueous solubility necessary for intravenous administration. This deficit was overcome by conversion of 4 to water-soluble pyridinium prodrugs. A two-step procedure was used to prepare a series of N-(acyloxyalkyl)pyridinium salts, all of which exhibited aqueous solubility of greater than 20 mg/mL. The rate of conversion of these prodrugs to 4 was faster in human plasma than in pH 7 aqueous buffer. This rate difference was shown to be due to serum enzymes since the conversion in plasma was significantly slower in the presence of a serine esterase inhibitor. A strong correlation between prodrug structure and buffer/plasma half-life was established. The N-(acetyloxymethyl)pyridinium prodrug 11 (ABT-299) is currently undergoing clinical evaluation for the treatment of sepsis.

MeSH terms

  • Animals
  • Male
  • Platelet Activating Factor / antagonists & inhibitors*
  • Prodrugs / chemical synthesis*
  • Prodrugs / pharmacology
  • Pyridinium Compounds / chemical synthesis*
  • Pyridinium Compounds / pharmacology
  • Rats
  • Rats, Sprague-Dawley
  • Solubility
  • Structure-Activity Relationship

Substances

  • Platelet Activating Factor
  • Prodrugs
  • Pyridinium Compounds