An adult-type metachromatic leukodystrophy caused by substitution of serine for glycine-122 in arylsulfatase A

Hum Genet. 1993 Nov;92(5):451-6. doi: 10.1007/BF00216449.

Abstract

Metachromatic leukodystrophy (MLD) is a lysosomal storage disease with autosomal recessive inheritance caused by a deficiency of the enzyme arylsulfatase A (ASA). We have identified a new mutation in the ASA gene of a patient with adult-type MLD. In this mutation, the glycine at position 122, a highly conserved residue in the AS gene family, was replaced by serine. In a transient expression study, COS cells transfected with the mutant cDNA carrying 122Gly-->Ser did not show an increase of ASA activity and produced little material immunoreactive to an anti-ASA antibody, despite normal mRNA levels.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Animals
  • Base Sequence
  • Cell Line
  • Cerebroside-Sulfatase / genetics*
  • Chlorocebus aethiops
  • DNA Mutational Analysis
  • DNA Primers
  • Female
  • Glycine / genetics
  • Humans
  • Kidney / cytology
  • Leukodystrophy, Metachromatic / genetics*
  • Molecular Sequence Data
  • Mutagenesis, Site-Directed
  • Point Mutation*
  • Polymorphism, Restriction Fragment Length
  • Serine / genetics
  • Transfection

Substances

  • DNA Primers
  • Serine
  • Cerebroside-Sulfatase
  • Glycine