Deletion of 19 base pairs in intron 13 of the gene for the pro alpha 2(I) chain of type-I procollagen (COL1A2) causes exon skipping in a proband with type-I osteogenesis imperfecta

Hum Genet. 1993 Apr;91(3):210-6. doi: 10.1007/BF00218258.

Abstract

Skin fibroblasts from a proband with mild osteogenesis imperfecta (type I) synthesized normal pro alpha 2(I) chains and shortened pro alpha 2(I) chains of type-I procollagen. The type-I collagen that contained the shortened alpha 2(I) chains was thermally unstable in that it was cleaved at 30 degrees C by a mixture of trypsin and chymotrypsin. The mutation generating the shortened pro alpha 2(I) chains was shown to be a deletion of 19 base pairs from +4 to +22 of intron 13 of the COL1A2 gene by sequencing of genomic DNA and allele-specific oligonucleotide hybridization. The same mutation was found in the proband's affected father. Probe-protection experiments with S1 nuclease demonstrated that about 88% of the RNA transcripts from the mutated allele were spliced by exon skipping from exon 12 to exon 14 and that about 12% of the RNA transcripts were normally spliced. There was no evidence for use of cryptic splice sites, even though two cryptic splice sites had more favorable statistical scores and delta G degree 37 values than the new site that was created by the mutation and that was used for splicing of 12% of the transcripts into a normal mRNA. Comparison of the results with observations on 17 previously reported mutations that produced in-frame deletions of amino acids from the triple-helical domain of type-I collagen indicated that deletions in the N-terminal half of the alpha 2(I) chain tended to produce milder phenotypes than similar deletions elsewhere in the alpha 1(I) or alpha 2(I) chains.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Adolescent
  • Base Composition
  • Base Sequence
  • Cells, Cultured
  • DNA
  • Exons
  • Female
  • Humans
  • Introns*
  • Male
  • Molecular Sequence Data
  • Mutation
  • Osteogenesis Imperfecta / genetics*
  • Procollagen / genetics*
  • RNA Splicing
  • Sequence Deletion*

Substances

  • Procollagen
  • DNA

Associated data

  • GENBANK/L13238
  • GENBANK/L13296
  • GENBANK/L13297
  • GENBANK/L14001
  • GENBANK/L14002
  • GENBANK/L14003
  • GENBANK/S59211
  • GENBANK/S59218
  • GENBANK/S70572
  • GENBANK/S70573