[Course of a case of Gaucher's disease type 1 treated over a year with glucocerebrosidase (Cérédase)]

Rev Med Interne. 1993;14(10):996. doi: 10.1016/s0248-8663(05)80114-6.
[Article in French]

Abstract

Gaucher's disease is caused by a deficiency of glucocerebrosidase. Enzyme replacement therapy with glucocerebrosidase (Ceredase) is available in France since 1991. We report the clinical effectiveness in a woman with type 1 Gaucher's disease treated with the enzyme for one year. Hepatomegaly regressed, bone pain decreased but improvement of severe skeletal manifestations were slow and incomplete.

Publication types

  • Case Reports
  • English Abstract

MeSH terms

  • Female
  • Gaucher Disease / drug therapy*
  • Glucosylceramidase / therapeutic use*
  • Humans
  • Middle Aged

Substances

  • Glucosylceramidase