The X-ray structure of (MeBm2t)1-cyclosporin complexed with cyclophilin A provides an explanation for its anomalously high immunosuppressive activity

Protein Eng. 1994 May;7(5):597-603. doi: 10.1093/protein/7.5.597.

Abstract

For most of the cyclosporin A (CsA) analogs, there is generally a good correlation between cyclophilin binding and immunosuppression. However, this relationship does not seem to hold for 4-[(E)-2-butenyl]-4,4,N-trimethyl-L-threonine1 (MeBm2t)1-CsA. Its affinity for cyclophilin was reported to be approximately 1% that of CsA and its immunosuppressive activity in vitro was shown to be approximately 30% that of CsA. We report here the crystal structure of a complex between recombinant human cyclophilin A (CypA) and (MeBm2t)1-CsA which has been determined by X-ray crystallography at 2.2 A resolution and refined to an R-factor of 16.3%. (MeBm2t)1-CsA shows a similar bound conformation and network of interactions to CypA as CsA. The measured lower affinity for CypA cannot therefore be explained by a different mode of binding. We propose that the poor affinity to CypA could be accounted for by the existence of an equilibrium in aqueous solution between a 'cyclophilin bound conformation' and a 'non-binding conformation' of (MeBm2t)1-CsA. The relatively high immunosuppressive activity is suggested to result from slight conformational differences observed in the effector domain.

MeSH terms

  • Amino Acid Isomerases / metabolism*
  • Amino Acid Sequence
  • Binding Sites
  • Carrier Proteins / metabolism*
  • Crystallization
  • Crystallography, X-Ray*
  • Cyclosporins / chemistry*
  • Cyclosporins / metabolism
  • Humans
  • Immunosuppression Therapy*
  • Models, Molecular
  • Molecular Conformation
  • Molecular Sequence Data
  • Molecular Structure
  • Peptidylprolyl Isomerase
  • Water / chemistry

Substances

  • Carrier Proteins
  • Cyclosporins
  • Water
  • cyclosporin A, 4-(2-butenyl)-4,4,N-trimethylthreonine(1)-
  • Amino Acid Isomerases
  • Peptidylprolyl Isomerase