Anti-Tac(Fab)-PE40, a recombinant double-chain immunotoxin which kills interleukin-2-receptor-bearing cells and induces complete remission in an in vivo tumor model

Int J Cancer. 1994 Jun 15;57(6):856-64. doi: 10.1002/ijc.2910570615.

Abstract

We have produced a single plasmid encoding both the heavy chain Fd domain (VH + CH1) of the anti-interleukin-2 receptor (IL2R) monoclonal antibody anti-Tac, and the anti-Tac light chain fused to PE40, a truncated derivative of Pseudomonas exotoxin. The active immunotoxin anti-Tac(Fab)-PE40 could be recovered from E. coli from either periplasm or renatured inclusion bodies. The double-chain immunotoxin was very cytotoxic toward IL2R-bearing cell lines, human activated T cells and fresh adult-T-cell-leukemia cells. The cytotoxicity was similar to that of anti-Tac(Fv)-PE40, the single-chain recombinant toxin containing only the variable domains of anti-Tac. IL2R-binding affinity was also equivalent to that of anti-Tac(Fv)-PE40, which is one-third that of anti-Tac. The serum half-life in mice was significantly prolonged as compared with anti-Tac(Fv)-PE40, with a beta phase of 430 vs. 57 minutes, but the LD50s were equivalent when the immunotoxins were administered in 3 daily doses. Anti-Tac(Fab)-PE40 was very cytotoxic in vitro toward transfected ATAC-4 carcinoma cells which express IL2Rs. In mice bearing ATAC-4 tumors, anti-Tac(Fab)-PE40 showed significant anti-tumor activity, inducing complete remissions in 80 and 100% of treated animals at approximately 7 and 14% respectively of the LD50. Anti-Tac(Fab)-PE40 was much more effective in vitro and in vivo than chemical conjugates between anti-Tac and truncated PE molecules. The recombinant Fab toxin should be studied further as potential treatment for IL2R-related malignancies, particularly if smaller recombinant immunotoxins have insufficient half-life in humans.

MeSH terms

  • ADP Ribose Transferases*
  • Animals
  • Antibodies, Monoclonal / therapeutic use*
  • Bacterial Toxins*
  • Base Sequence
  • Exotoxins / administration & dosage*
  • Exotoxins / chemistry
  • Exotoxins / toxicity
  • Humans
  • Immunotoxins / chemistry*
  • Immunotoxins / toxicity
  • Mice
  • Mice, Nude
  • Molecular Sequence Data
  • Neoplasm Transplantation
  • Neoplasms, Experimental / drug therapy*
  • Oligodeoxyribonucleotides / chemistry
  • Pseudomonas aeruginosa Exotoxin A
  • Receptors, Interleukin-2 / immunology*
  • Recombinant Fusion Proteins / chemistry
  • Recombinant Fusion Proteins / pharmacokinetics
  • Transplantation, Heterologous
  • Tumor Cells, Cultured / drug effects
  • Virulence Factors*

Substances

  • Antibodies, Monoclonal
  • Bacterial Toxins
  • Exotoxins
  • Immunotoxins
  • Oligodeoxyribonucleotides
  • Receptors, Interleukin-2
  • Recombinant Fusion Proteins
  • Virulence Factors
  • ADP Ribose Transferases