Smith-Lemli-Opitz syndrome: biochemical before clinical diagnosis; early dietary management

Am J Med Genet. 1994 May 1;50(4):375-6. doi: 10.1002/ajmg.1320500415.

Abstract

Pursuit of a possible metabolic basis for an unrecognized pattern of multiple congenital anomalies in a newborn girl led to the detection of a huge elevation of plasma 7-dehydrocholesterol at age 8 months. The biochemical findings and the evolving clinical picture led to the diagnosis of Smith-Lemli-Opitz syndrome at age 11 months. High cholesterol diet may have improved the rate of developmental progress.

Publication types

  • Case Reports
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Abnormalities, Multiple / diet therapy
  • Abnormalities, Multiple / metabolism*
  • Bile Acids and Salts / urine
  • Cholesterol / biosynthesis*
  • Cholesterol, Dietary / therapeutic use*
  • Dehydrocholesterols / blood
  • Face / abnormalities
  • Female
  • Humans
  • Infant
  • Intellectual Disability / diet therapy
  • Intellectual Disability / metabolism*
  • Lipid Metabolism, Inborn Errors / diet therapy*
  • Lipid Metabolism, Inborn Errors / metabolism
  • Microcephaly
  • Syndrome

Substances

  • Bile Acids and Salts
  • Cholesterol, Dietary
  • Dehydrocholesterols
  • Cholesterol
  • 7-dehydrocholesterol