Presymptomatic diagnosis of SMA III by genotype analysis

Am J Med Genet. 1993 Feb 1;45(3):408-11. doi: 10.1002/ajmg.1320450331.

Abstract

Linkage analysis and prenatal prediction in families segregating autosomal recessive spinal muscular atrophy (SMA) has become feasible since the assignment of the locus responsible for type I-III SMA to region 5q12-q13.3. We have performed a segregation study of SMA in Italian families using molecular probes and highly informative PCR-based polymorphic markers. In one family, a 7-year-old boy affected with type III SMA and an 8-year-old apparently healthy brother had identical haplotypes. These findings prompted us to reexamine the apparently unaffected child. His neurological exam was normal. However, the electromyography (EMG) showed a pattern consistent with chronic SMA. To our knowledge this is the first example of presymptomatic diagnosis of SMA based on genotype analysis.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Base Sequence
  • Child
  • DNA / genetics
  • Electromyography
  • Genotype
  • Humans
  • Male
  • Molecular Sequence Data
  • Muscular Atrophy, Spinal / classification
  • Muscular Atrophy, Spinal / diagnosis*
  • Muscular Atrophy, Spinal / genetics*
  • Pedigree

Substances

  • DNA

Grants and funding