General overgrowth in the fragile X syndrome: variability in the phenotypic expression of the FMR1 gene mutation

J Med Genet. 1995 Oct;32(10):764-9. doi: 10.1136/jmg.32.10.764.

Abstract

The fragile X syndrome, which often presents in childhood with overgrowth, may in some cases show some diagnostic overlap with classical Sotos syndrome. We describe four fragile X patients with general overgrowth, all of whom are from families with other affected relatives who show the classic Martin-Bell phenotype. Molecular studies of the FMR1 gene in all cases showed the typical full mutation as seen in males affected by the fragile X syndrome. Endocrine studies were unremarkable, except in one case where there were raised levels of insulin-like growth factor-I (IGF-I) and insulin-like growth factor binding protein-3 (IGFBP-3)

These cases illustrate the clinical variability of the fragile X syndrome and the necessity of performing analysis of the FMR1 gene in mentally retarded patients presenting with general overgrowth.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Child, Preschool
  • Fragile X Mental Retardation Protein
  • Fragile X Syndrome / complications
  • Fragile X Syndrome / genetics*
  • Fragile X Syndrome / physiopathology
  • Growth Disorders / etiology
  • Growth Disorders / genetics*
  • Growth Disorders / physiopathology
  • Humans
  • Insulin-Like Growth Factor Binding Protein 3 / metabolism
  • Insulin-Like Growth Factor I / metabolism
  • Male
  • Mutation
  • Nerve Tissue Proteins / genetics*
  • Pedigree
  • Phenotype
  • RNA-Binding Proteins*

Substances

  • FMR1 protein, human
  • Insulin-Like Growth Factor Binding Protein 3
  • Nerve Tissue Proteins
  • RNA-Binding Proteins
  • Fragile X Mental Retardation Protein
  • Insulin-Like Growth Factor I