Abstract
Tyrosinemia type III, caused by deficiency of 4-hydroxyphenylpyruvate dioxygenase, is a rare disorder of tyrosine catabolism. Primary 4-hydroxyphenylpyruvate dioxygenase deficiency has been described in only three patients. The biochemical phenotype shows hypertyrosinemia and elevated urinary excretion of 4-hydroxyphenyl derivatives. We report the clinical and biochemical findings and the results of long-term follow-up in a new patient with this disorder presenting with severe mental retardation and neurological abnormalities. The clinical phenotype is compared with those reported in the three previously described patients.
MeSH terms
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4-Hydroxyphenylpyruvate Dioxygenase / deficiency*
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Adolescent
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Amino Acid Metabolism, Inborn Errors / diagnosis*
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Amino Acid Metabolism, Inborn Errors / diet therapy
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Amino Acid Metabolism, Inborn Errors / enzymology
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Amino Acids / administration & dosage
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Biopsy, Needle
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Child
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Child, Preschool
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Drug Combinations
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Follow-Up Studies
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Humans
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Intellectual Disability / diagnosis
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Intellectual Disability / diet therapy
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Intellectual Disability / enzymology
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Liver / enzymology
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Liver / pathology
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Male
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Minerals / administration & dosage
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Neurologic Examination
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Tyrosine / administration & dosage
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Tyrosine / blood*
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Vitamins / administration & dosage
Substances
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Amino Acids
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Drug Combinations
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Milupa
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Minerals
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Vitamins
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Tyrosine
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4-Hydroxyphenylpyruvate Dioxygenase