[Gene therapy in rheumatoid polyarthritis: perspectives]

Presse Med. 1998 Mar 28;27(12):580-2.
[Article in French]

Abstract

THE CONCEPT OF GENE THERAPY: Gene therapy is applicable in diseases involving several genes such as rheumatoid arthritis. Gene transfer is the insertion in vivo of genetic material necessary to produce a molecule with therapeutic action. This strategy is currently in experimental stages; feasibility studies in humans are in the preliminary stage. SEVERAL TARGETS: In experimental models of rheumatoid arthritis, the most widely studied target genes are those which code for inflammation inhibitors such as IL-1 receptor antagonists or anti-inflammatory cytokines (IL-4, IL-10, IL-13). Another interesting target would concern genes coding for molecules inhibiting joint destruction (for example metalloprotease inhibitors). VECTORS: The development of high-performance vectors (both viral and nonviral vectors) will greatly improve the expected benefit/risk potential of gene therapy in general. IN RHEUMATOID ARTHRITIS: The particular problem in rheumatoid arthritis is the choice of the transfection site. An articular site would require multiple injections in the different affected joints. A systemic approach would take into account the general disseminated nature of the disease.

Publication types

  • English Abstract
  • Review

MeSH terms

  • Animals
  • Arthritis, Rheumatoid / therapy*
  • Cytokines / genetics
  • Cytokines / therapeutic use
  • Disease Models, Animal
  • Feasibility Studies
  • Gene Transfer Techniques
  • Genetic Therapy*
  • Genetic Vectors
  • Humans
  • Injections
  • Injections, Intra-Articular
  • Receptors, Interleukin-1 / antagonists & inhibitors
  • Receptors, Interleukin-1 / genetics
  • Risk Assessment
  • Transfection

Substances

  • Cytokines
  • Receptors, Interleukin-1