An accurate stable isotope dilution gas chromatographic-mass spectrometric approach to the diagnosis of guanidinoacetate methyltransferase deficiency

J Pharm Biomed Anal. 1998 Dec;18(4-5):659-65. doi: 10.1016/s0731-7085(98)00280-5.

Abstract

A gas chromatography-mass spectrometry (GC-MS) method is described for the quantification of guanidinoacetate in different body fluids, using a two step derivatisation procedure which involves a reaction with hexafluoroacetylacetone to form a bis(trifluoromethyl)pyrimidine ring structure followed by a reaction with pentafluorobenzyl bromide. 13C2-labelled guanidinoacetate is used as an internal standard. Bis(trifluoromethyl)pyrimidine pentafluorobenzyl derivatives were separated on a polar capillary GC-column and were quantified using negative chemical ionisation mass fragmentography. The detection limit of the method is 1 pmol guanidinoacetate in a 100 microl sample. Control values were obtained for urine (53.9 +/- 25.9 mmol mol(-1) creatinine), plasma (1.08 +/- 0.31 micromol l(-1)), cerebrospinal fluid (CSF) (0.114 +/- 0.068 micromol l(-1)) and amniotic fluid (3.44 +/- 0.64 micromol l(-1)). The applicability of the method is illustrated by the determination of guanidinoacetate in urine, plasma and CSF of a patient affected with guanidinoacetate methyltransferase deficiency. In all body fluids of this patient, guanidinoacetate was highly elevated.

MeSH terms

  • Amino Acid Metabolism, Inborn Errors / diagnosis*
  • Child
  • Creatine / biosynthesis
  • Gas Chromatography-Mass Spectrometry / methods*
  • Glycine / analogs & derivatives
  • Glycine / analysis
  • Guanidinoacetate N-Methyltransferase
  • Humans
  • Methyltransferases / deficiency*
  • Radioisotope Dilution Technique

Substances

  • Methyltransferases
  • Guanidinoacetate N-Methyltransferase
  • glycocyamine
  • Creatine
  • Glycine