Tumor cell-specific transgene expression prevents liver toxicity of the adeno-HSVtk/GCV approach

Gene Ther. 1998 Oct;5(10):1363-71. doi: 10.1038/sj.gt.3300728.

Abstract

Treatment of colorectal liver metastases with the HSVtk/GCV approach and adenoviral vectors is highly toxic. We present a nontoxic alternative using the cell type-specific CEA promoter instead of the widely used hCMV immediate-early promoter to drive tk gene expression in the context of a recombinant adenovirus. Analysis of CEA promoter-dependent tk gene expression showed significant activity of this promoter in several human and rat tumor-derived cell lines but not in rat primary hepatocytes and in mouse liver, whereas the CMV promoter was highly active in all cell types and tissues investigated. CEA promoter-dependent tk gene expression was sufficient to kill 100% of cancer cells in vitro, even if less than 10% were infected by the adenoviral vector, indicating a significant bystander effect. Moreover, treatment of subcutaneous tumors in SCID mice with Ad.CEA-tk led to a several-fold reduction of tumor growth, and tail vein injection of a high dose of Ad.CEA-tk caused no side-effects in the liver. The CMV promoter was more potent than the CEA promoter in mediating GCV sensitivity to cancer cells in vitro and in vivo, but even a 20-fold reduction of the dose of Ad.CMV-tk did not prevent its liver cell toxicity after systemic application to mice and still resulted in the death of all animals within 4 days after the start of GCV treatment. These results indicate that restriction of tk gene expression to tumor cells in the liver prevents systemic toxicity. Moreover, the CEA promoter is a safe and efficient tool for tumor cell-specific expression of suicide genes in the liver.

MeSH terms

  • Adenoviridae
  • Animals
  • Antimetabolites / adverse effects
  • Antimetabolites / therapeutic use
  • Blotting, Southern
  • Carcinoembryonic Antigen / genetics*
  • Colorectal Neoplasms / drug therapy
  • Colorectal Neoplasms / therapy*
  • Combined Modality Therapy
  • Ganciclovir / adverse effects
  • Ganciclovir / therapeutic use
  • Gene Expression
  • Genetic Therapy / methods*
  • Genetic Vectors
  • Liver / drug effects
  • Liver Neoplasms / drug therapy
  • Liver Neoplasms / secondary*
  • Liver Neoplasms / therapy*
  • Mice
  • Mice, SCID
  • Promoter Regions, Genetic*
  • Thymidine Kinase / genetics
  • Transfection / methods
  • Transgenes

Substances

  • Antimetabolites
  • Carcinoembryonic Antigen
  • Thymidine Kinase
  • Ganciclovir