Intracerebroventricular 2-hydroxypropyl-γ-cyclodextrin alleviates hepatic manifestations without distributing to the liver in a murine model of Niemann-Pick disease type C.
Yamada Y, Ishitsuka Y, Fukaura-Nishizawa M, Kawata T, Ishii A, Shirakawa A, Sakai T, Tanaka M, Kondo Y, Takeo T, Nakagata N, Motoyama K, Higashi T, Arima H, Seki T, Kurauchi Y, Katsuki H, Higaki K, Ikeda R, Matsuo M, Era T, Irie T.
Yamada Y, et al. Among authors: shirakawa a.
Life Sci. 2024 Aug 1;350:122776. doi: 10.1016/j.lfs.2024.122776. Epub 2024 Jun 7.
Life Sci. 2024.
PMID: 38852794