Event-free survival of maralixibat-treated patients with Alagille syndrome compared to a real-world cohort from GALA.
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Hansen BE, et al. Among authors: carvalho e.
Hepatology. 2024 Jun 1;79(6):1279-1292. doi: 10.1097/HEP.0000000000000727. Epub 2023 Dec 25.
Hepatology. 2024.
PMID: 38146932
Free PMC article.