Ex Vivo Gene Therapy Treats Bone Complications of Mucopolysaccharidosis Type II Mouse Models through Bone Remodeling Reactivation.
Wada M, Shimada Y, Iizuka S, Ishii N, Hiraki H, Tachibana T, Maeda K, Saito M, Arakawa S, Ishimoto T, Nakano T, Ida H, Ohashi T, Kobayashi H.
Wada M, et al. Among authors: iizuka s.
Mol Ther Methods Clin Dev. 2020 Sep 20;19:261-274. doi: 10.1016/j.omtm.2020.09.012. eCollection 2020 Dec 11.
Mol Ther Methods Clin Dev. 2020.
PMID: 33102618
Free PMC article.