Biodistribution and Tolerability of AAV-PHP.B-CBh-SMN1 in Wistar Han Rats and Cynomolgus Macaques Reveal Different Toxicologic Profiles.
Palazzi X, Pardo ID, Sirivelu MP, Newman L, Kumpf SW, Qian J, Franks T, Lopes S, Liu J, Monarski L, Casinghino S, Ritenour C, Ritenour H, Dubois C, Olson J, Graves J, Alexander KE, Coskran T, Lanz TA, Brady J, McCarty D, Suryanarayan S, Whiteley LO.
Palazzi X, et al. Among authors: liu j.
Hum Gene Ther. 2022 Feb;33(3-4):175-187. doi: 10.1089/hum.2021.116.
Hum Gene Ther. 2022.
PMID: 34931542
Free PMC article.