Charrier S - Search Results

1

Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome.

Hacein-Bey Abina S, Gaspar HB, Blondeau J, Caccavelli L, Charrier S, Buckland K, Picard C, Six E, Himoudi N, Gilmour K, McNicol AM, Hara H, Xu-Bayford J, Rivat C, Touzot F, Mavilio F, Lim A, Treluyer JM, Héritier S, Lefrère F, Magalon J, Pengue-Koyi I, Honnet G, Blanche S, Sherman EA, Male F, Berry C, Malani N, Bushman FD, Fischer A, Thrasher AJ, Galy A, Cavazzana M. Hacein-Bey Abina S, et al. Among authors: charrier s. JAMA. 2015 Apr 21;313(15):1550-63. doi: 10.1001/jama.2015.3253. JAMA. 2015. PMID: 25898053 Free PMC article. Clinical Trial.

2

Wiskott-Aldrich syndrome protein-deficient hematopoietic cells can be efficiently mobilized by granulocyte colony-stimulating factor.

Charrier S, Blundell M, Cédrone G, Louache F, Vainchenker W, Thrasher AJ, Galy A. Charrier S, et al. Haematologica. 2013 Aug;98(8):1300-8. doi: 10.3324/haematol.2012.077040. Epub 2013 Feb 26. Haematologica. 2013. PMID: 23445877 Free PMC article.

3

Validation of a mutated PRE sequence allowing high and sustained transgene expression while abrogating WHV-X protein synthesis: application to the gene therapy of WAS.

Zanta-Boussif MA, Charrier S, Brice-Ouzet A, Martin S, Opolon P, Thrasher AJ, Hope TJ, Galy A. Zanta-Boussif MA, et al. Among authors: charrier s. Gene Ther. 2009 May;16(5):605-19. doi: 10.1038/gt.2009.3. Epub 2009 Mar 5. Gene Ther. 2009. PMID: 19262615

4

A partial down-regulation of WASP is sufficient to inhibit podosome formation in dendritic cells.

Olivier A, Jeanson-Leh L, Bouma G, Compagno D, Blondeau J, Seye K, Charrier S, Burns S, Thrasher AJ, Danos O, Vainchenker W, Galy A. Olivier A, et al. Among authors: charrier s. Mol Ther. 2006 Apr;13(4):729-37. doi: 10.1016/j.ymthe.2005.11.003. Epub 2005 Dec 15. Mol Ther. 2006. PMID: 16360341 Free article.

5

Diverse genomic integration of a lentiviral vector developed for the treatment of Wiskott-Aldrich syndrome.

Mantovani J, Charrier S, Eckenberg R, Saurin W, Danos O, Perea J, Galy A. Mantovani J, et al. Among authors: charrier s. J Gene Med. 2009 Aug;11(8):645-54. doi: 10.1002/jgm.1346. J Gene Med. 2009. PMID: 19455589

6

Preclinical Development of a Lentiviral Vector for Gene Therapy of X-Linked Severe Combined Immunodeficiency.

Poletti V, Charrier S, Corre G, Gjata B, Vignaud A, Zhang F, Rothe M, Schambach A, Gaspar HB, Thrasher AJ, Mavilio F. Poletti V, et al. Among authors: charrier s. Mol Ther Methods Clin Dev. 2018 Mar 10;9:257-269. doi: 10.1016/j.omtm.2018.03.002. eCollection 2018 Jun 15. Mol Ther Methods Clin Dev. 2018. PMID: 29707600 Free PMC article.

7

Biosafety Studies of a Clinically Applicable Lentiviral Vector for the Gene Therapy of Artemis-SCID.

Charrier S, Lagresle-Peyrou C, Poletti V, Rothe M, Cédrone G, Gjata B, Mavilio F, Fischer A, Schambach A, de Villartay JP, Cavazzana M, Hacein-Bey-Abina S, Galy A. Charrier S, et al. Mol Ther Methods Clin Dev. 2019 Sep 13;15:232-245. doi: 10.1016/j.omtm.2019.08.014. eCollection 2019 Dec 13. Mol Ther Methods Clin Dev. 2019. PMID: 31720302 Free PMC article.

8

A lentiviral vector encoding the human Wiskott-Aldrich syndrome protein corrects immune and cytoskeletal defects in WASP knockout mice.

Charrier S, Stockholm D, Seye K, Opolon P, Taveau M, Gross DA, Bucher-Laurent S, Delenda C, Vainchenker W, Danos O, Galy A. Charrier S, et al. Gene Ther. 2005 Apr;12(7):597-606. doi: 10.1038/sj.gt.3302440. Gene Ther. 2005. PMID: 15616597

9

Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients.

Charrier S, Dupré L, Scaramuzza S, Jeanson-Leh L, Blundell MP, Danos O, Cattaneo F, Aiuti A, Eckenberg R, Thrasher AJ, Roncarolo MG, Galy A. Charrier S, et al. Gene Ther. 2007 Mar;14(5):415-28. doi: 10.1038/sj.gt.3302863. Epub 2006 Oct 19. Gene Ther. 2007. PMID: 17051251

10

The c.273+11dup genetic change in the WAS gene is a functionally neutral polymorphism.

Jeanson-Leh L, Charrier S, Proust A, Bilhou-Nabéra C, Favier R, Deswarte C, Bordigoni P, Galy A, Delaunay J. Jeanson-Leh L, et al. Among authors: charrier s. Eur J Haematol. 2011 Oct;87(4):366-71. doi: 10.1111/j.1600-0609.2011.01674.x. Epub 2011 Aug 11. Eur J Haematol. 2011. PMID: 21711396

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