Targeting proximal tubule mitochondrial dysfunction attenuates the renal disease of methylmalonic acidemia.
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Proc Natl Acad Sci U S A. 2013 Aug 13;110(33):13552-7. doi: 10.1073/pnas.1302764110. Epub 2013 Jul 29.
Proc Natl Acad Sci U S A. 2013.
PMID: 23898205
Free PMC article.
Clinical Trial.