Pharmacological enhancement of KCC2 gene expression exerts therapeutic effects on human Rett syndrome neurons and Mecp2 mutant mice.
Sci Transl Med. 2019 Jul 31;11(503):eaau0164. doi: 10.1126/scitranslmed.aau0164.
Sci Transl Med. 2019.
PMID: 31366578
Free PMC article.