Mireault AA - Search Results

1

In vivo non-invasive monitoring of dystrophin correction in a new Duchenne muscular dystrophy reporter mouse.

Amoasii L, Li H, Zhang Y, Min YL, Sanchez-Ortiz E, Shelton JM, Long C, Mireault AA, Bhattacharyya S, McAnally JR, Bassel-Duby R, Olson EN. Amoasii L, et al. Among authors: mireault aa. Nat Commun. 2019 Oct 4;10(1):4537. doi: 10.1038/s41467-019-12335-x. Nat Commun. 2019. PMID: 31586095 Free PMC article.

2

Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA.

Long C, McAnally JR, Shelton JM, Mireault AA, Bassel-Duby R, Olson EN. Long C, et al. Among authors: mireault aa. Science. 2014 Sep 5;345(6201):1184-1188. doi: 10.1126/science.1254445. Epub 2014 Aug 14. Science. 2014. PMID: 25123483 Free PMC article.

3

Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy.

Long C, Amoasii L, Mireault AA, McAnally JR, Li H, Sanchez-Ortiz E, Bhattacharyya S, Shelton JM, Bassel-Duby R, Olson EN. Long C, et al. Among authors: mireault aa. Science. 2016 Jan 22;351(6271):400-3. doi: 10.1126/science.aad5725. Epub 2015 Dec 31. Science. 2016. PMID: 26721683 Free PMC article.

4

Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy.

Amoasii L, Long C, Li H, Mireault AA, Shelton JM, Sanchez-Ortiz E, McAnally JR, Bhattacharyya S, Schmidt F, Grimm D, Hauschka SD, Bassel-Duby R, Olson EN. Amoasii L, et al. Among authors: mireault aa. Sci Transl Med. 2017 Nov 29;9(418):eaan8081. doi: 10.1126/scitranslmed.aan8081. Sci Transl Med. 2017. PMID: 29187645 Free PMC article.

5

Gene editing restores dystrophin expression in a canine model of Duchenne muscular dystrophy.

Amoasii L, Hildyard JCW, Li H, Sanchez-Ortiz E, Mireault A, Caballero D, Harron R, Stathopoulou TR, Massey C, Shelton JM, Bassel-Duby R, Piercy RJ, Olson EN. Amoasii L, et al. Science. 2018 Oct 5;362(6410):86-91. doi: 10.1126/science.aau1549. Epub 2018 Aug 30. Science. 2018. PMID: 30166439 Free PMC article.

6

CRISPR-Cas9 corrects Duchenne muscular dystrophy exon 44 deletion mutations in mice and human cells.

Min YL, Li H, Rodriguez-Caycedo C, Mireault AA, Huang J, Shelton JM, McAnally JR, Amoasii L, Mammen PPA, Bassel-Duby R, Olson EN. Min YL, et al. Among authors: mireault aa. Sci Adv. 2019 Mar 6;5(3):eaav4324. doi: 10.1126/sciadv.aav4324. eCollection 2019 Mar. Sci Adv. 2019. PMID: 30854433 Free PMC article.

7

Enhanced CRISPR-Cas9 correction of Duchenne muscular dystrophy in mice by a self-complementary AAV delivery system.

Zhang Y, Li H, Min YL, Sanchez-Ortiz E, Huang J, Mireault AA, Shelton JM, Kim J, Mammen PPA, Bassel-Duby R, Olson EN. Zhang Y, et al. Among authors: mireault aa. Sci Adv. 2020 Feb 19;6(8):eaay6812. doi: 10.1126/sciadv.aay6812. eCollection 2020 Feb. Sci Adv. 2020. PMID: 32128412 Free PMC article.

8

Precise correction of Duchenne muscular dystrophy exon deletion mutations by base and prime editing.

Chemello F, Chai AC, Li H, Rodriguez-Caycedo C, Sanchez-Ortiz E, Atmanli A, Mireault AA, Liu N, Bassel-Duby R, Olson EN. Chemello F, et al. Among authors: mireault aa. Sci Adv. 2021 Apr 30;7(18):eabg4910. doi: 10.1126/sciadv.abg4910. Print 2021 Apr. Sci Adv. 2021. PMID: 33931459 Free PMC article.

9

Correction of Three Prominent Mutations in Mouse and Human Models of Duchenne Muscular Dystrophy by Single-Cut Genome Editing.

Min YL, Chemello F, Li H, Rodriguez-Caycedo C, Sanchez-Ortiz E, Mireault AA, McAnally JR, Shelton JM, Zhang Y, Bassel-Duby R, Olson EN. Min YL, et al. Among authors: mireault aa. Mol Ther. 2020 Sep 2;28(9):2044-2055. doi: 10.1016/j.ymthe.2020.05.024. Epub 2020 May 30. Mol Ther. 2020. PMID: 32892813 Free PMC article.

10

A consolidated AAV system for single-cut CRISPR correction of a common Duchenne muscular dystrophy mutation.

Zhang Y, Nishiyama T, Li H, Huang J, Atmanli A, Sanchez-Ortiz E, Wang Z, Mireault AA, Mammen PPA, Bassel-Duby R, Olson EN. Zhang Y, et al. Among authors: mireault aa. Mol Ther Methods Clin Dev. 2021 Jun 4;22:122-132. doi: 10.1016/j.omtm.2021.05.014. eCollection 2021 Sep 10. Mol Ther Methods Clin Dev. 2021. PMID: 34485599 Free PMC article.

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