Flotte TR - Search Results

1

Limb Perfusion Delivery of a rAAV1 Alpha-1 Antitrypsin Vector in Non-Human Primates Is Safe but Insufficient for Therapy.

Pires-Ferreira D, Reil D, Tang Q, Blackwood M, Gallagher T, Keeler AM, Chichester JA, Vyhnal KK, Lindborg JA, Benson J, Fu D, Flotte TR, Gruntman AM. Pires-Ferreira D, et al. Among authors: flotte tr. Genes (Basel). 2024 Sep 10;15(9):1188. doi: 10.3390/genes15091188. Genes (Basel). 2024. PMID: 39336779 Free PMC article.

2

Neuroimaging Applications for the Delivery and Monitoring of Gene Therapy for Central Nervous System Diseases.

Daci R, Gray-Edwards H, Shazeeb MS, Vardar Z, Vachha B, Cataltepe OI, Flotte TR. Daci R, et al. Among authors: flotte tr. Hum Gene Ther. 2024 Nov;35(21-22):886-895. doi: 10.1089/hum.2024.057. Epub 2024 Nov 8. Hum Gene Ther. 2024. PMID: 39323316 Review.

3

The Road Less Traveled: Slow but Steady Progress Toward Cystic Fibrosis Gene Therapy by the UK Respiratory Gene Therapy Consortium.

Flotte TR. Flotte TR. Am J Respir Crit Care Med. 2024 Dec 15;210(12):1387-1389. doi: 10.1164/rccm.202408-1516ED. Am J Respir Crit Care Med. 2024. PMID: 39265185 No abstract available.

4

AAV5 Delivery of CRISPR/Cas9 Mediates Genome Editing in the Lungs of Young Rhesus Monkeys.

Liang SQ, Navia AW, Ramseier M, Zhou X, Martinez M, Lee C, Zhou C, Wu J, Xie J, Su Q, Wang D, Flotte TR, Anderson DG, Tarantal AF, Shalek AK, Gao G, Xue W. Liang SQ, et al. Among authors: flotte tr. Hum Gene Ther. 2024 Oct;35(19-20):814-824. doi: 10.1089/hum.2024.035. Epub 2024 Jul 3. Hum Gene Ther. 2024. PMID: 38767512

5

Intrathecal gene therapy for neurologic disease in humans.

Flotte TR. Flotte TR. Mol Ther. 2024 May 1;32(5):1185-1186. doi: 10.1016/j.ymthe.2024.04.013. Epub 2024 Apr 24. Mol Ther. 2024. PMID: 38663405 No abstract available.

6

Kenneth I. Berns, MD, PhD [1938-2024].

Byrne BJ, Flotte TR, Herzog RW, Srivastava A. Byrne BJ, et al. Among authors: flotte tr. Hum Gene Ther. 2024 Mar;35(5-6):133-134. doi: 10.1089/hum.2024.29266.kib. Hum Gene Ther. 2024. PMID: 38497910 No abstract available.

7

Biodistribution and safety of a single rAAV3B-AAT vector for silencing and replacement of alpha-1 antitrypsin in Cynomolgus macaques.

Blackwood M, Gruntman AM, Tang Q, Pires-Ferreira D, Reil D, Kondratov O, Marsic D, Zolotukhin S, Gernoux G, Keeler AM, Mueller C, Flotte TR. Blackwood M, et al. Among authors: flotte tr. Mol Ther Methods Clin Dev. 2024 Jan 30;32(1):101200. doi: 10.1016/j.omtm.2024.101200. eCollection 2024 Mar 14. Mol Ther Methods Clin Dev. 2024. PMID: 38445045 Free PMC article.

8

Delivery of Adeno-Associated Virus Vectors to the Central Nervous System for Correction of Single Gene Disorders.

Daci R, Flotte TR. Daci R, et al. Among authors: flotte tr. Int J Mol Sci. 2024 Jan 15;25(2):1050. doi: 10.3390/ijms25021050. Int J Mol Sci. 2024. PMID: 38256124 Free PMC article. Review.

9

Approaches to Therapeutic Gene Editing in Alpha-1 Antitrypsin Deficiency.

Gruntman AM, Xue W, Flotte TR. Gruntman AM, et al. Among authors: flotte tr. Methods Mol Biol. 2024;2750:11-17. doi: 10.1007/978-1-0716-3605-3_2. Methods Mol Biol. 2024. PMID: 38108963

10

Alpha-1 Antitrypsin Deficiency.

Gruntman AM, Xue W, Flotte TR. Gruntman AM, et al. Among authors: flotte tr. Methods Mol Biol. 2024;2750:1-7. doi: 10.1007/978-1-0716-3605-3_1. Methods Mol Biol. 2024. PMID: 38108962

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