AAV2/9-mediated silencing of PMP22 prevents the development of pathological features in a rat model of Charcot-Marie-Tooth disease 1 A.
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Nat Commun. 2021 Apr 21;12(1):2356. doi: 10.1038/s41467-021-22593-3.
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PMID: 33883545
Free PMC article.