Semirational bioengineering of AAV vectors with increased potency and specificity for systemic gene therapy of muscle disorders.
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Sci Adv. 2022 Sep 23;8(38):eabn4704. doi: 10.1126/sciadv.abn4704. Epub 2022 Sep 21.
Sci Adv. 2022.
PMID: 36129972
Free PMC article.