Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia.
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Thompson AA, et al. Among authors: semeraro m.
N Engl J Med. 2018 Apr 19;378(16):1479-1493. doi: 10.1056/NEJMoa1705342.
N Engl J Med. 2018.
PMID: 29669226
Free article.
Clinical Trial.