Transfer of SCN1A to the brain of adolescent mouse model of Dravet syndrome improves epileptic, motor, and behavioral manifestations.
Mora-Jimenez L, Valencia M, Sanchez-Carpintero R, Tønnesen J, Fadila S, Rubinstein M, Gonzalez-Aparicio M, Bunuales M, Fernandez-Pierola E, Nicolas MJ, Puerta E, Miguelez C, Minguez PG, Lumbreras S, Gonzalez-Aseguinolaza G, Ricobaraza A, Hernandez-Alcoceba R.
Mora-Jimenez L, et al. Among authors: ricobaraza a.
Mol Ther Nucleic Acids. 2021 Aug 19;25:585-602. doi: 10.1016/j.omtn.2021.08.003. eCollection 2021 Sep 3.
Mol Ther Nucleic Acids. 2021.
PMID: 34589280
Free PMC article.