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Assessment of Safety and Biodistribution of AAVrh.10hCLN2 Following Intracisternal Administration in Nonhuman Primates for the Treatment of CLN2 Batten Disease.
De BP, Rosenberg JB, Selvan N, Wilson I, Yusufzai N, Greco A, Kaminsky SM, Heier LA, Ricart Arbona RJ, Miranda IC, Monette S, Nair A, Khanna R, Crystal RG, Sondhi D. De BP, et al. Among authors: khanna r. Hum Gene Ther. 2023 Sep;34(17-18):905-916. doi: 10.1089/hum.2023.067. Hum Gene Ther. 2023. PMID: 37624739 Free PMC article.
Expression and processing of mature human frataxin after gene therapy in mice.
Rojsajjakul T, Selvan N, De B, Rosenberg JB, Kaminsky SM, Sondhi D, Janki P, Crystal RG, Mesaros C, Khanna R, Blair IA. Rojsajjakul T, et al. Among authors: khanna r. Sci Rep. 2024 Apr 10;14(1):8391. doi: 10.1038/s41598-024-59060-0. Sci Rep. 2024. PMID: 38600238 Free PMC article.
Identification of Safe and Effective Intravenous Dose of AAVrh.10hFXN to Treat the Cardiac Manifestations of Friedreich's Ataxia.
Munoz-Zuluaga C, Gertz M, Yost-Bido M, Greco A, Gorman N, Chen A, Kooner V, Rosenberg JB, De BP, Kaminsky SM, Borczuk A, Ricart Arbona RJ, Martin HR, Monette S, Khanna R, Barth JA, Crystal RG, Sondhi D. Munoz-Zuluaga C, et al. Among authors: khanna r. Hum Gene Ther. 2023 Jul;34(13-14):605-615. doi: 10.1089/hum.2023.020. Epub 2023 Jul 4. Hum Gene Ther. 2023. PMID: 37166361 Free PMC article.
Expression and processing of mature human frataxin after gene therapy in mice.
Rojsajjakul T, Selvan N, De B, Rosenberg JB, Kaminsky SM, Sondhi D, Janki P, Crystal RG, Mesaros C, Khanna R, Blair IA. Rojsajjakul T, et al. Among authors: khanna r. Res Sq [Preprint]. 2023 Dec 28:rs.3.rs-3788652. doi: 10.21203/rs.3.rs-3788652/v1. Res Sq. 2023. Update in: Sci Rep. 2024 Apr 10;14(1):8391. doi: 10.1038/s41598-024-59060-0 PMID: 38234818 Free PMC article. Updated. Preprint.
Transforming Households with Refraction and Innovative Financial Technology (THRIFT): study protocol for a randomised controlled trial of vision interventions and online banking among the elderly in Kurigram.
Shitol SA, Aftab IB, Piyasena P, Lohfeld L, Rayasam S, Challa N, Sangani P, Sigwadhi LN, Rahman HMM, Khanna RC, Chan VF, Barua M, Pant S, Adhvaryu A, Nyshadham A, Sarker M, Mettla AL, Haque E, MacKenzie G, Alam S, Gudwin E, Clarke M, Shonchoy A, Rabbani A, Congdon N. Shitol SA, et al. Among authors: khanna rc. BMJ Open. 2024 Dec 23;14(12):e085083. doi: 10.1136/bmjopen-2024-085083. BMJ Open. 2024. PMID: 39719288 Free PMC article. Clinical Trial.
Neuropeptide Y and Pain: Insights from Brain Research.
Nelson TS, Allen HN, Khanna R. Nelson TS, et al. Among authors: khanna r. ACS Pharmacol Transl Sci. 2024 Nov 2;7(12):3718-3728. doi: 10.1021/acsptsci.4c00333. eCollection 2024 Dec 13. ACS Pharmacol Transl Sci. 2024. PMID: 39698268 Review.
STABLE trial of spectacle provision and driving safety among myopic motorcycle users in Vietnam: study protocol for a stepped-wedge, cluster randomised trial.
Le VC, To KG, Le VD, Nguyen L, MacKenzie G, Sigwadhi LN, Piyasena P, Tran M, Chan VF, Khanna RC, Clarke M, Lohfeld L, Dickey H, Azuara-Blanco A, Mettla AL, Rayasam S, Doan HTN, Van Do D, Le PH, Klauer C, Hanowski R, Bowden Z, Murphy L, Thompson J, McMullan S, McDowell C, Narayanan R, Little JA, Ha HT, Yoon S, Goel R, Luong L, Nguyen X, Congdon N. Le VC, et al. Among authors: khanna rc. Trials. 2024 Dec 18;25(1):825. doi: 10.1186/s13063-024-08644-2. Trials. 2024. PMID: 39695859 Free PMC article.
2,136 results