CRISPR-based gene editing enables FOXP3 gene repair in IPEX patient cells.
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Sci Adv. 2020 May 6;6(19):eaaz0571. doi: 10.1126/sciadv.aaz0571. eCollection 2020 May.
Sci Adv. 2020.
PMID: 32494707
Free PMC article.