Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation

Search Page

Filters

My Custom Filters

Publication date

Text availability

Article attribute

Article type

Additional filters

Article Language

Species

Sex

Age

Other

Search Results

3,851 results

Filters applied: . Clear all
Results are displayed in a computed author sort order. The Publication Date timeline is not available.
Page 1
Uptake of orphan drugs in the WHO essential medicines lists.
Costa E, Moja L, Wirtz VJ, van den Ham HA, Huttner B, Magrini N, Leufkens HG. Costa E, et al. Bull World Health Organ. 2024 Jan 1;102(1):22-31. doi: 10.2471/BLT.23.289731. Epub 2023 Oct 31. Bull World Health Organ. 2024. PMID: 38164340 Free PMC article.
Emergent treatments for β-thalassemia and orphan drug legislations.
Costa E, Cappellini MD, Rivella S, Chilin A, Alessi E, Riccaboni M, Leufkens HGM, Luzzatto L. Costa E, et al. Drug Discov Today. 2022 Nov;27(11):103342. doi: 10.1016/j.drudis.2022.103342. Epub 2022 Sep 1. Drug Discov Today. 2022. PMID: 36058507 Free article. Review.
Globalization in clinical drug development for sickle cell disease.
Costa E, Ware RE, Tshilolo L, Makani J, Leufkens HGM, Luzzatto L. Costa E, et al. Am J Hematol. 2025 Jan;100(1):4-9. doi: 10.1002/ajh.27525. Epub 2024 Nov 12. Am J Hematol. 2025. PMID: 39530361 Free PMC article. No abstract available.
[Considerations on limits and profits of registries].
Addis A, Costa E, De Palma R, Magrini N, Marata AM, Martelli L, Papini D, Traversa G; Aziende Farmaceutiche partecipanti ai lavori del PRIER II. Addis A, et al. Among authors: costa e. Recenti Prog Med. 2015 Sep;106(9):425-35. doi: 10.1701/1996.21590. Recenti Prog Med. 2015. PMID: 26418504 Italian.
Orphan drugs - Authors' reply.
Luzzatto L, Costa E, Schieppati A, Remuzzi G. Luzzatto L, et al. Among authors: costa e. Lancet. 2019 Apr 20;393(10181):1595-1596. doi: 10.1016/S0140-6736(19)30014-5. Lancet. 2019. PMID: 31007199 No abstract available.
Outrageous prices of orphan drugs: a call for collaboration.
Luzzatto L, Hyry HI, Schieppati A, Costa E, Simoens S, Schaefer F, Roos JCP, Merlini G, Kääriäinen H, Garattini S, Hollak CE, Remuzzi G; Second Workshop on Orphan Drugs participants. Luzzatto L, et al. Among authors: costa e. Lancet. 2018 Sep 1;392(10149):791-794. doi: 10.1016/S0140-6736(18)31069-9. Epub 2018 Jul 20. Lancet. 2018. PMID: 30037734 No abstract available.
3,851 results