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Advancing rare disease treatment: EMA's decade-long insights into engineered adoptive cell therapy for rare cancers and orphan designation.
Kalland ME, Pose-Boirazian T, Palomo GM, Naumann-Winter F, Costa E, Matusevicius D, Duarte DM, Malikova E, Vitezic D, Larsson K, Magrelli A, Stoyanova-Beninska V, Mariz S. Kalland ME, et al. Among authors: costa e. Gene Ther. 2024 Jul;31(7-8):366-377. doi: 10.1038/s41434-024-00446-0. Epub 2024 Mar 14. Gene Ther. 2024. PMID: 38480914 Free PMC article. Review.
Uptake of orphan drugs in the WHO essential medicines lists.
Costa E, Moja L, Wirtz VJ, van den Ham HA, Huttner B, Magrini N, Leufkens HG. Costa E, et al. Bull World Health Organ. 2024 Jan 1;102(1):22-31. doi: 10.2471/BLT.23.289731. Epub 2023 Oct 31. Bull World Health Organ. 2024. PMID: 38164340 Free PMC article.
Emergent treatments for β-thalassemia and orphan drug legislations.
Costa E, Cappellini MD, Rivella S, Chilin A, Alessi E, Riccaboni M, Leufkens HGM, Luzzatto L. Costa E, et al. Drug Discov Today. 2022 Nov;27(11):103342. doi: 10.1016/j.drudis.2022.103342. Epub 2022 Sep 1. Drug Discov Today. 2022. PMID: 36058507 Free article. Review.
Adoption of Digital Therapeutics in Europe.
Fassbender A, Donde S, Silva M, Friganovic A, Stievano A, Costa E, Winders T, van Vugt J. Fassbender A, et al. Among authors: costa e. Ther Clin Risk Manag. 2024 Dec 27;20:939-954. doi: 10.2147/TCRM.S489873. eCollection 2024. Ther Clin Risk Manag. 2024. PMID: 39741688 Free PMC article. Review.
3,844 results