Ensuring Stakeholder Feedback in the Design and Conduct of Clinical Trials for Rare Diseases: ISCTM Position Paper of the Orphan Disease Working Group.
Pandina GJ, Busner J, Kempf L, Fallon J, Alphs LD, Acosta MT, Berger AK, Day S, Dunn J, Villalta-Gil V, Grabb MC, Horrigan JP, Jacobson W, Kando JC, Macek TA, Singh MK, Stanford AD, Domingo SZ.
Pandina GJ, et al. Among authors: grabb mc.
Innov Clin Neurosci. 2024 Mar 1;21(1-3):52-60. eCollection 2024 Jan-Mar.
Innov Clin Neurosci. 2024.
PMID: 38495603
Free PMC article.
Review.