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Engineering Memory T Cells as a platform for Long-Term Enzyme Replacement Therapy in Lysosomal Storage Disorders.
Laoharawee K, Kleinboehl EW, Jensen JD, Peterson JJ, Slipek NJ, Wick BJ, Johnson MJ, Webber BR, Moriarity BS. Laoharawee K, et al. bioRxiv [Preprint]. 2024 Apr 28:2024.04.23.590790. doi: 10.1101/2024.04.23.590790. bioRxiv. 2024. Update in: Mol Ther. 2024 Nov 6;32(11):3865-3878. doi: 10.1016/j.ymthe.2024.09.033 PMID: 38712248 Free PMC article. Updated. Preprint.
Precision Enhancement of CAR-NK Cells through Non-Viral Engineering and Highly Multiplexed Base Editing.
Wang M, Krueger JB, Gilkey AK, Stelljes EM, Kluesner MG, Pomeroy EJ, Skeate JG, Slipek NJ, Lahr WS, Vázquez PNC, Zhao Y, Eaton EJ, Laoharawee K, Webber BR, Moriarity BS. Wang M, et al. Among authors: laoharawee k. bioRxiv [Preprint]. 2024 Mar 8:2024.03.05.582637. doi: 10.1101/2024.03.05.582637. bioRxiv. 2024. PMID: 38496503 Free PMC article. Preprint.
Non-invasive intravenous administration of AAV9 transducing iduronate sulfatase leads to global metabolic correction and prevention of neurologic deficits in a mouse model of Hunter syndrome.
Laoharawee K, Podetz-Pedersen KM, Nguyen TT, Singh SM, Smith MC, Belur LR, Low WC, Kozarsky KF, McIvor RS. Laoharawee K, et al. Mol Genet Metab Rep. 2023 Jan 20;34:100956. doi: 10.1016/j.ymgmr.2023.100956. eCollection 2023 Mar. Mol Genet Metab Rep. 2023. PMID: 36704405 Free PMC article.
Correction of Fanconi Anemia Mutations Using Digital Genome Engineering.
Sipe CJ, Kluesner MG, Bingea SP, Lahr WS, Andrew AA, Wang M, DeFeo AP, Hinkel TL, Laoharawee K, Wagner JE, MacMillan ML, Vercellotti GM, Tolar J, Osborn MJ, McIvor RS, Webber BR, Moriarity BS. Sipe CJ, et al. Among authors: laoharawee k. Int J Mol Sci. 2022 Jul 29;23(15):8416. doi: 10.3390/ijms23158416. Int J Mol Sci. 2022. PMID: 35955545 Free PMC article.
Primary B cell engineering for therapeutic research.
Kleinboehl E, Laoharawee K, Moriarity BS. Kleinboehl E, et al. Among authors: laoharawee k. Trends Mol Med. 2022 Jun;28(6):528-529. doi: 10.1016/j.molmed.2022.03.007. Epub 2022 Apr 13. Trends Mol Med. 2022. PMID: 35430120 Free PMC article. No abstract available.
18 results