An erythroid-specific lentiviral vector improves anemia and iron metabolism in a new model of XLSA.
Castruccio Castracani C, Breda L, Papp TE, Guerra A, Radaelli E, Assenmacher CA, Finesso G, Mui BL, Tam YK, Fontana S, Riganti C, Fiorito V, Petrillo S, Tolosano E, Parhiz H, Rivella S.
Castruccio Castracani C, et al. Among authors: papp te.
Blood. 2025 Jan 2;145(1):98-113. doi: 10.1182/blood.2024025846.
Blood. 2025.
PMID: 39656107