Splice-correcting oligonucleotides restore BTK function in X-linked agammaglobulinemia model.
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Bestas B, et al. Among authors: blomberg ke.
J Clin Invest. 2014 Sep;124(9):4067-81. doi: 10.1172/JCI76175. Epub 2014 Aug 8.
J Clin Invest. 2014.
PMID: 25105368
Free PMC article.