Targeting the transferrin receptor to transport antisense oligonucleotides across the mammalian blood-brain barrier.
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Sci Transl Med. 2024 Aug 14;16(760):eadi2245. doi: 10.1126/scitranslmed.adi2245. Epub 2024 Aug 14.
Sci Transl Med. 2024.
PMID: 39141703