Amphiphilic shuttle peptide delivers base editor ribonucleoprotein to correct the CFTR R553X mutation in well-differentiated airway epithelial cells.
Kulhankova K, Cheng AX, Traore S, Auger M, Pelletier M, Hervault M, Wells KD, Green JA, Byrne A, Nelson B, Sponchiado M, Boosani C, Heffner CS, Snow KJ, Murray SA, Villacreses RA, Rector MV, Gansemer ND, Stoltz DA, Allamargot C, Couture F, Hemez C, Hallée S, Barbeau X, Harvey M, Lauvaux C, Gaillet B, Newby GA, Liu DR, McCray PB Jr, Guay D.
Kulhankova K, et al. Among authors: stoltz da.
Nucleic Acids Res. 2024 Oct 28;52(19):11911-11925. doi: 10.1093/nar/gkae819.
Nucleic Acids Res. 2024.
PMID: 39315713
Free PMC article.