Dual-targeting CRISPR-CasRx reduces C9orf72 ALS/FTD sense and antisense repeat RNAs in vitro and in vivo.
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Kempthorne L, et al. Among authors: fisher a.
Nat Commun. 2025 Jan 8;16(1):459. doi: 10.1038/s41467-024-55550-x.
Nat Commun. 2025.
PMID: 39779704
Free article.