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Year Number of Results
2012 1
2013 5
2014 5
2015 8
2016 4
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2018 4
2019 1
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37 results

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Page 1
Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial.
Russell S, Bennett J, Wellman JA, Chung DC, Yu ZF, Tillman A, Wittes J, Pappas J, Elci O, McCague S, Cross D, Marshall KA, Walshire J, Kehoe TL, Reichert H, Davis M, Raffini L, George LA, Hudson FP, Dingfield L, Zhu X, Haller JA, Sohn EH, Mahajan VB, Pfeifer W, Weckmann M, Johnson C, Gewaily D, Drack A, Stone E, Wachtel K, Simonelli F, Leroy BP, Wright JF, High KA, Maguire AM. Russell S, et al. Lancet. 2017 Aug 26;390(10097):849-860. doi: 10.1016/S0140-6736(17)31868-8. Epub 2017 Jul 14. Lancet. 2017. PMID: 28712537 Free PMC article. Clinical Trial.
What Is Next for Retinal Gene Therapy?
Vandenberghe LH. Vandenberghe LH. Cold Spring Harb Perspect Med. 2015 Apr 15;5(10):a017442. doi: 10.1101/cshperspect.a017442. Cold Spring Harb Perspect Med. 2015. PMID: 25877395 Free PMC article. Review.
Adeno-associated virus: fit to serve.
Zinn E, Vandenberghe LH. Zinn E, et al. Curr Opin Virol. 2014 Oct;8:90-7. doi: 10.1016/j.coviro.2014.07.008. Epub 2014 Aug 13. Curr Opin Virol. 2014. PMID: 25128609 Free PMC article. Review.
Promising and delivering gene therapies for vision loss.
Carvalho LS, Vandenberghe LH. Carvalho LS, et al. Vision Res. 2015 Jun;111(Pt B):124-33. doi: 10.1016/j.visres.2014.07.013. Epub 2014 Aug 2. Vision Res. 2015. PMID: 25094052 Free PMC article. Review.
Immunology of AAV-Mediated Gene Transfer in the Eye.
Willett K, Bennett J. Willett K, et al. Front Immunol. 2013 Aug 30;4:261. doi: 10.3389/fimmu.2013.00261. eCollection 2013. Front Immunol. 2013. PMID: 24009613 Free PMC article. Review.
Institutional Conflict of Interest.
Bennett J. Bennett J. JAMA Ophthalmol. 2016 Nov 1;134(11):1334-1335. doi: 10.1001/jamaophthalmol.2016.3248. JAMA Ophthalmol. 2016. PMID: 27583791 Free PMC article. No abstract available.
Perspectives on best practices for gene therapy programs.
Cheever TR, Berkley D, Braun S, Brown RH, Byrne BJ, Chamberlain JS, Cwik V, Duan D, Federoff HJ, High KA, Kaspar BK, Klinger KW, Larkindale J, Lincecum J, Mavilio F, McDonald CL, McLaughlin J, Weiss McLeod B, Mendell JR, Nuckolls G, Stedman HH, Tagle DA, Vandenberghe LH, Wang H, Wernett PJ, Wilson JM, Porter JD, Gubitz AK. Cheever TR, et al. Hum Gene Ther. 2015 Mar;26(3):127-33. doi: 10.1089/hum.2014.147. Epub 2015 Mar 3. Hum Gene Ther. 2015. PMID: 25654329 Free PMC article.
37 results