Combination effects of SMAC mimetic birinapant with TNFα, TRAIL, and docetaxel in preclinical models of HNSCC

Laryngoscope. 2015 Mar;125(3):E118-24. doi: 10.1002/lary.25056. Epub 2014 Nov 28.

Abstract

Objectives/hypothesis: Head and neck squamous cell carcinoma (HNSCC) cells are resistant to cell death induced by tumor necrosis factor ligands such as tumor necrosis factor α (TNFα) or TNF-related apoptosis-inducing ligand (TRAIL) and cytotoxic chemotherapies. Recently, genetic alterations in cell death pathways, including inhibitor of apoptosis proteins, have been demonstrated in HNSCC. We investigated the effects of birinapant, a novel, second mitochondria-derived activator of caspases (SMAC)-mimetic that targets inhibitor of apoptosis proteins, alone and in combination with TNFα, TRAIL, or chemotherapy docetaxel.

Study design: Experimental study using human HNSCC cell lines in vitro and xenograft mouse model in vivo.

Methods: A panel of HNSCC cell lines with varying genetic alterations in cell death pathway components were treated with birinapant ± TNFα, TRAIL, and docetaxel and were assessed for effects on cell density, cell cycle, and death. Synergism was determined at varying concentrations of treatments using the Chou-Talalay method. Combination studies using birinapant ± docetaxel were performed in a xenograft mouse model.

Results: Birinapant, alone or in combination with TNFα or TRAIL, decreased cell density in cell lines, with IC50 s ranging from 0.5 nM to > 1 µM. Birinapant alone or with TNF significantly increased subG0 cell death in different lines. Docetaxel showed synergism with birinapant ± TNFα in vitro. Birinapant monotherapy-inhibited growth in a tumor xenograft model resistant to docetaxel, and combination treatment further delayed growth.

Conclusions: Birinapant alone or in combination with TNFα or TRAIL and docetaxel decreased cell density, increased cell death, and displayed antitumor activity in a preclinical HNSCC xenograft exhibiting aberrations in cell death pathway components and docetaxel resistance.

Keywords: Inhibitor of Apoptosis; cell death; second mitochondria-derived activator of caspases; squamous carcinoma.

Publication types

  • Research Support, N.I.H., Intramural

MeSH terms

  • Animals
  • Antineoplastic Agents / pharmacology
  • Apoptosis
  • Apoptosis Regulatory Proteins
  • Carcinoma, Squamous Cell / drug therapy*
  • Carcinoma, Squamous Cell / metabolism
  • Carcinoma, Squamous Cell / pathology
  • Cell Count
  • Cell Line, Tumor
  • Cell Proliferation
  • Dipeptides / pharmacology*
  • Docetaxel
  • Drug Therapy, Combination
  • Female
  • Flow Cytometry
  • Head and Neck Neoplasms / drug therapy*
  • Head and Neck Neoplasms / metabolism
  • Head and Neck Neoplasms / pathology
  • Humans
  • Indoles / pharmacology*
  • Intracellular Signaling Peptides and Proteins / pharmacology*
  • Mice
  • Mitochondrial Proteins / pharmacology*
  • Neoplasms, Experimental*
  • Squamous Cell Carcinoma of Head and Neck
  • TNF-Related Apoptosis-Inducing Ligand / pharmacology*
  • Taxoids / pharmacology*
  • Tumor Necrosis Factor-alpha / pharmacology*

Substances

  • Antineoplastic Agents
  • Apoptosis Regulatory Proteins
  • DIABLO protein, human
  • Dipeptides
  • Indoles
  • Intracellular Signaling Peptides and Proteins
  • Mitochondrial Proteins
  • TNF-Related Apoptosis-Inducing Ligand
  • Taxoids
  • Tumor Necrosis Factor-alpha
  • Docetaxel
  • birinapant