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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
1992 1
1993 1
2002 3
2003 5
2004 2
2007 1
2008 3
2009 3
2010 5
2011 3
2012 4
2013 3
2016 2
2018 7
2019 4
2020 1
2021 3
2022 5
2023 3
2024 4

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57 results

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Page 1
Trial of Antisense Oligonucleotide Tofersen for SOD1 ALS.
Miller TM, Cudkowicz ME, Genge A, Shaw PJ, Sobue G, Bucelli RC, Chiò A, Van Damme P, Ludolph AC, Glass JD, Andrews JA, Babu S, Benatar M, McDermott CJ, Cochrane T, Chary S, Chew S, Zhu H, Wu F, Nestorov I, Graham D, Sun P, McNeill M, Fanning L, Ferguson TA, Fradette S; VALOR and OLE Working Group. Miller TM, et al. N Engl J Med. 2022 Sep 22;387(12):1099-1110. doi: 10.1056/NEJMoa2204705. N Engl J Med. 2022. PMID: 36129998 Free article. Clinical Trial.
Base editing of haematopoietic stem cells rescues sickle cell disease in mice.
Newby GA, Yen JS, Woodard KJ, Mayuranathan T, Lazzarotto CR, Li Y, Sheppard-Tillman H, Porter SN, Yao Y, Mayberry K, Everette KA, Jang Y, Podracky CJ, Thaman E, Lechauve C, Sharma A, Henderson JM, Richter MF, Zhao KT, Miller SM, Wang T, Koblan LW, McCaffrey AP, Tisdale JF, Kalfa TA, Pruett-Miller SM, Tsai SQ, Weiss MJ, Liu DR. Newby GA, et al. Among authors: mccaffrey ap. Nature. 2021 Jul;595(7866):295-302. doi: 10.1038/s41586-021-03609-w. Epub 2021 Jun 2. Nature. 2021. PMID: 34079130 Free PMC article.
Design and Statistical Innovations in a Platform Trial for Amyotrophic Lateral Sclerosis.
Quintana M, Saville BR, Vestrucci M, Detry MA, Chibnik L, Shefner J, Berry JD, Chase M, Andrews J, Sherman AV, Yu H, Drake K, Cudkowicz M, Paganoni S, Macklin EA; HEALEY ALS Platform Trial Study Group. Quintana M, et al. Ann Neurol. 2023 Sep;94(3):547-560. doi: 10.1002/ana.26714. Epub 2023 Jun 22. Ann Neurol. 2023. PMID: 37245090
Efficacy and Safety of NVX-CoV2373 in Adults in the United States and Mexico.
Dunkle LM, Kotloff KL, Gay CL, Áñez G, Adelglass JM, Barrat Hernández AQ, Harper WL, Duncanson DM, McArthur MA, Florescu DF, McClelland RS, Garcia-Fragoso V, Riesenberg RA, Musante DB, Fried DL, Safirstein BE, McKenzie M, Jeanfreau RJ, Kingsley JK, Henderson JA, Lane DC, Ruíz-Palacios GM, Corey L, Neuzil KM, Coombs RW, Greninger AL, Hutter J, Ake JA, Smith K, Woo W, Cho I, Glenn GM, Dubovsky F; 2019nCoV-301 Study Group. Dunkle LM, et al. N Engl J Med. 2022 Feb 10;386(6):531-543. doi: 10.1056/NEJMoa2116185. Epub 2021 Dec 15. N Engl J Med. 2022. PMID: 34910859 Free PMC article. Clinical Trial.
Adaptive Platform Trials to Transform Amyotrophic Lateral Sclerosis Therapy Development.
Paganoni S, Berry JD, Quintana M, Macklin E, Saville BR, Detry MA, Chase M, Sherman AV, Yu H, Drake K, Andrews J, Shefner J, Chibnik LB, Vestrucci M, Cudkowicz ME; Healey ALS Platform Trial Study Group. Paganoni S, et al. Ann Neurol. 2022 Feb;91(2):165-175. doi: 10.1002/ana.26285. Epub 2022 Jan 10. Ann Neurol. 2022. PMID: 34935174 Review.
Insights to COVID-19 vaccine delivery: Results from a survey of 27 countries.
Mathur I, Church R, Ruisch A, Noyes K, McCaffrey A, Griffiths U, Oyatoye I, Brenzel L, Walker D, Suharlim C. Mathur I, et al. Among authors: mccaffrey a. Vaccine. 2023 Oct 13;41(43):6406-6410. doi: 10.1016/j.vaccine.2023.08.087. Epub 2023 Sep 23. Vaccine. 2023. PMID: 37743118 Free article.
Multicenter expanded access program for access to investigational products for amyotrophic lateral sclerosis.
Neel DV, Baselga-Garriga C, Benson M, Keegan M, Chase M, D'Agostino D, Drake K, Hagar JL, Hasenoehrl MG, Kulesa-Kelley J, Leite A, Mohapatra S, Portaro SM, Pothier LM, Rosenthal J, Sherman AV, Yu H, McCaffrey A, Ho D, Luppino S, Bedlack R, Heitzman D, Ajroud-Driss S, Katz J, Felice K, Whitaker C, Ladha S, Alameda G, Locatelli E, Qureshi IA, Hotchkin MT, Hayden MR, Cudkowicz ME, Babu S, Berry JD, Paganoni S. Neel DV, et al. Among authors: mccaffrey a. Muscle Nerve. 2024 Aug;70(2):232-239. doi: 10.1002/mus.28169. Epub 2024 Jun 6. Muscle Nerve. 2024. PMID: 38842106
Global VAX: A U.S. contribution to global COVID-19 vaccination efforts, 2021-2023.
Dahl BA, Tritter B, Butryn D, Dahlke M, Browning S, Gelting R, Fleming M, Ortiz N, Labrador J, Novak R, Fitter D, Bell E, McGuire M, Rosenbaum R, Pulwer R, Wun J, McCaffrey A, Chowdhury M, Parks N, Cunningham M, Mounts A, Curry D, Richardson D, Grant G. Dahl BA, et al. Among authors: mccaffrey a. Vaccine. 2024 Sep 17;42 Suppl 3(Suppl 3):125827. doi: 10.1016/j.vaccine.2024.03.054. Epub 2024 Mar 23. Vaccine. 2024. PMID: 38523004 Free PMC article.
Advances in microRNAs: implications for gene therapists.
Marquez RT, McCaffrey AP. Marquez RT, et al. Among authors: mccaffrey ap. Hum Gene Ther. 2008 Jan;19(1):27-38. doi: 10.1089/hum.2007.147. Hum Gene Ther. 2008. PMID: 18092919 Free PMC article. Review.
57 results