Novel mutation of the P0 extracellular domain causes a Déjérine-Sottas syndrome

J Neurol Neurosurg Psychiatry. 1999 Mar;66(3):386-9. doi: 10.1136/jnnp.66.3.386.

Abstract

A patient is described with a Déjérine-Sottas syndrome caused by a novel heterozygous Cys(98)Tyr mutation in the extracellular domain of the major peripheral myelin protein zero (P0ex). Homotypical interactions between P0ex tetramers of apposed extracellular faces of the Schwann cell membrane play a crucial part in myelin compaction. The amino acid change disrupts a unique disulphide bond that stabilises the immunoglobulin-like structure of P0ex and it is predicted to cause severe dehypomyelination through dominant negative effects on the wild type protein.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Electrophoresis, Gel, Pulsed-Field
  • Genetic Carrier Screening
  • Hereditary Sensory and Motor Neuropathy / genetics*
  • Hereditary Sensory and Motor Neuropathy / pathology
  • Humans
  • Male
  • Mutation
  • Myelin P0 Protein / genetics*
  • Syndrome

Substances

  • Myelin P0 Protein

Grants and funding