Circular permutation of the granulocyte colony-stimulating factor receptor agonist domain of myelopoietin

Biochemistry. 1999 Apr 6;38(14):4564-71. doi: 10.1021/bi982225g.

Abstract

Myelopoietins (MPOs) are a family of engineered dual interleukin-3 (IL-3) and granulocyte colony-stimulating factor (G-CSF) receptor agonists that are superior in comparison to the single agonists in their ability to promote the growth and maturation of hematopoietic cells of the myeloid lineage. A series of MPO molecules were created which incorporated circularly permuted G-CSF (cpG-CSF) sequences with an IL-3 receptor (IL-3R) agonist moiety attached at locations that correspond to the loops that connect the helices of the G-CSF four-helix bundle structure. The cpG-CSF linkage sites (using the original sequence numbering) were residue 39, which is at the beginning of the first loop connecting helices 1 and 2; residue 97, which is in the turn connecting helices 2 and 3; and residues 126, 133, and 142, which are at the beginning, middle, and end, respectively, of the loop connecting helices 3 and 4. The N- and C-terminal helices of each cpG-CSF domain were constrained, either by direct linkage of the termini (L0) or by replacement of the amino-terminal 10-residue segment with a seven-residue linker composed of SGGSGGS (L1). All of the MPO molecules stimulated the proliferation of both IL-3-dependent (EC50 = 13-95 pM) and G-CSF-dependent (EC50 = 35-710 pM) cell lines. MPOs with the IL-3R agonist domain linked to cpG-CSFs in the first (residue 39) or second (residue 133) long overhand loops were found by CD spectroscopy to have helical contents similar to that expected for a protein comprised of two linked four-helix bundles. The MPOs retained the ability to bind to the IL-3R with affinities similar to that of the parental MPO. Using both a cell surface competitive binding assay and surface plasmon resonance detection of binding kinetics, the MPOs were found to bind to the G-CSF receptor with low nanomolar affinities, similar to that of G-CSF(S17). In a study of isolated cpG-CSF domains [Feng, Y., et al. (1999) Biochemistry 38, 4553-4563], domains with the L1 linker had lower G-CSF receptor-mediated proliferative activities and conformational stabilities than those which had the L0 linker. A similar trend was found for the MPOs in which the G-CSFR agonist activity is mostly a property of the cpG-CSF domain. Important exceptions were found in which the linkage to the IL-3R agonist domain either restored (e.g., attachment at residue 142) or further decreased (linkage at residue 39) the G-CSFR-mediated proliferative activity. MPO in which the IL-3R agonist domain is attached to the cpG-CSF(L1)[133/132] domain was shown to be more potent than the coaddition of the IL-3R agonist and G-CSF in stimulating the production of CFU-GM colonies in a human bone marrow-derived CD34+ colony-forming unit assay. Several MPOs also had decreased proinflammatory activity in a leukotriene C4 release assay using N-formyl-Met-Leu-Phe-primed human monocytes. It was found that circular permutation of the G-CSF domain can alter the ratio of G-CSFR:IL-3R agonist activities, demonstrating that it is a useful tool in engineering chimeric proteins with therapeutic potential.

MeSH terms

  • Amino Acid Sequence
  • Animals
  • Binding Sites / genetics
  • Cell Division / drug effects
  • Cell Line
  • Circular Dichroism
  • Granulocyte Colony-Stimulating Factor
  • Hematopoietic Cell Growth Factors / pharmacology*
  • Humans
  • Interleukin-3
  • Leukotriene C4 / blood
  • Leukotriene C4 / metabolism
  • Mice
  • Models, Molecular
  • Molecular Sequence Data
  • Peptide Fragments / agonists
  • Peptide Fragments / genetics*
  • Peptide Fragments / metabolism
  • Protein Engineering* / methods
  • Protein Structure, Tertiary
  • Receptors, Granulocyte Colony-Stimulating Factor / agonists*
  • Receptors, Granulocyte Colony-Stimulating Factor / genetics*
  • Receptors, Granulocyte Colony-Stimulating Factor / metabolism
  • Receptors, Interleukin-3 / agonists
  • Receptors, Interleukin-3 / genetics
  • Receptors, Interleukin-3 / metabolism
  • Recombinant Fusion Proteins* / agonists
  • Recombinant Fusion Proteins* / chemical synthesis*
  • Recombinant Fusion Proteins* / metabolism
  • Recombinant Proteins
  • Surface Plasmon Resonance

Substances

  • Hematopoietic Cell Growth Factors
  • Interleukin-3
  • Peptide Fragments
  • Receptors, Granulocyte Colony-Stimulating Factor
  • Receptors, Interleukin-3
  • Recombinant Fusion Proteins
  • Recombinant Proteins
  • myelopoietin
  • Granulocyte Colony-Stimulating Factor
  • Leukotriene C4